New York, NY, Jan. 23, 2023 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) has selected 15-year-old Leah Zelaya from Brooklyn, New York, as its 2023 MDA National…
No added benefit is proven, however, for older patients (types 2 and 3) and for presymptomatic infants whose genetic defects were detected in newborn screening. For onasemnogene…
In August 2020, the FDA approved the usage of risdiplam (Evrysdi) to treat SMA for adults and children two months and older. ‘Risdiplam helped improving motor functions among children with…