Taysha Gene Therapies Presents Preclinical Data on TSHA-102 for Rett Syndrome…
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Browsing Tag
Rett
Rett Syndrome Market is expected to hit USD 515.06 Mn by 2029 at a CAGR of 10.23…
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Taysha Gene Therapies Announces Presentation on New Preclinical Data for TSHA-102 in…
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PharmaTher Holdings Announces FDA Grant of Orphan Drug Designation to KETARX™…
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DepYmed Receives European Medicines Agency Orphan Drug Designation for Its Lead…
FARMINGDALE, N.Y., Nov. 16, 2022 (GLOBE NEWSWIRE) -- DepYmed, Inc. (“DepYmed” or the “Company”) is a preclinical stage pharmaceutical company focused on developing transformative…
Beyond neurons: How cells called astrocytes contribute to brain disorders: New…
Neurons often get most of the credit for keeping our brains sharp and functioning -- as well as most of the blame when it comes to brain diseases. But star-shaped cells called astrocytes,…
Advanced imaging reveals mired migration of neurons in Rett syndrome lab models
Using an innovative microscopy method, scientists at The Picower Institute for Learning and Memory at MIT observed how newborn neurons struggle to reach their proper places in advanced human…
Organoids reveal similarities between myotonic dystrophy type 1 and Rett syndrome:…
Myotonic dystrophy type 1 (DM1) is the most common form of muscular dystrophy, characterized by progressive muscle wasting and weakness and caused by abnormally repetitive DNA segments that…
Trofinetide Shows Promise in Rett Syndrome
The investigational drug trofinetide showed modest benefit in girls and young women with Rett syndrome, the phase III LAVENDER study…
Reduced inhibition of hippocampal neurons impairs long-term memory recall in Rett…
An exciting study by researchers in the laboratory of Dr. Huda Zoghbi, distinguished service professor at Baylor College of Medicine and director of the Jan and Dan Duncan Neurological…