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Interim results from the RESPOND study show improved motor function in most participants treated with SPINRAZA after Zolgensma® (onasemnogene abeparvovec)Biogen also reported new real-world…

BOSTON -- Upper limb function and walking ability were largely preserved in adults with spinal muscular atrophy (SMA) treated…

No added benefit is proven, however, for older patients (types 2 and 3) and for presymptomatic infants whose genetic defects were detected in newborn screening. For onasemnogene…