Dystrophy

FDA grants orphan drug designation for MetrioPharm’s lead compound MP1032 for the treatment of Duchenne muscular dystrophy (DMD)DMD is a designated orphan disease in both Europe and the…

A team of researchers at the University of Houston College of Pharmacy is reporting that by manipulating TAK1, a signaling protein that plays an important role in development of the immune…

<!-- Name:DistributionId Value:8844182 --> <!-- Name:EnableQuoteCarouselOnPnr Value:False -->…

Reshma Ramachandran, MD,…

<!-- Name:DistributionId Value:8842463 --> <!-- Name:EnableQuoteCarouselOnPnr Value:False -->…

FDA advisors narrowly supported accelerated approval for Sarepta Therapeutics'…

<!-- Name:DistributionId Value:8837554 --> <!-- Name:EnableQuoteCarouselOnPnr Value:False -->…

<!-- Name:DistributionId Value:8832867 --> <!-- Name:EnableQuoteCarouselOnPnr Value:False -->…

<!-- Name:DistributionId Value:8825434 --> <!-- Name:EnableQuoteCarouselOnPnr Value:False -->…

<!-- Name:DistributionId Value:8823719 --> <!-- Name:EnableQuoteCarouselOnPnr Value:False -->…